NTSAD officially has launched a webinar series to bring the experts to the community to discuss topics ranging from research advances to issues that impact the family. As is custom, NTSAD will post the recording of each webinar without the Q&A that follows each presentation.  

Wednesday, August 7, 2019

IntraBio and IB1001 Clinical Trials  Panelists: Taylor Fields, Senior VP, IntraBio Tatiana Bremova, MD, PhD, University Hospital Bern, Switzerland A presentation about IntraBio's compound, IB1001, the clinical trials in the US and Europe, and the hope that it has a positive impact on the GM2 Gangliosidoses (Tay-Sachs and Sandhoff). Facilitated by Staci Kallish, DO, NTSAD Board president. pdf Acetyl-DL-leucine in Niemann-Pick (Type C) - paper (587 KB) pdf Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials - paper (2.91 MB)

 

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Is there a particular topic you'd like to see discussed in a webinar format? Feel free to send an email to NTSAD This email address is being protected from spambots. You need JavaScript enabled to view it..