Research abstracts, publications, NTSAD initiatives, and Tay Sachs Gene Therapy Consortium (TSGT)
This folder contains slide presentations, handouts and other materials relating to the Research Update session at the NTSAD Annual Family Conferences. Please do not alter, publish or copy without permission from NTSAD.
The goal of the subcommittee is to evaluate clinical trials or other proposed therapies for Tay-Sachs, GM1, Sandhoff, Canavan and related diseases to educate families regarding trials and how to assess a proposed new or untested therapy. Papers written on different topics of therapies and/or clinical trials will be saved in this folder.