Leading the Fight to treat and cure
Tay-Sachs, Canavan, Sandhoff, GM1 and related diseases


Are we close to a cure?

NTSAD is dedicated to finding a cure for Tay-Sachs, Sandhoff, Canavan, GM-1 and all the related diseases. Founded over 50 years ago, NTSAD has been at the forefront of advancing and supporting breakthrough research through the Research Initiative and collaborative programs.

This is a very exciting time in Tay-Sachs and related diseases research. The Tay-Sachs Gene Therapy Consortium program has already shown excellent results in animal models and is driving toward initiating human clinical trials.

For Families

Overview of Potential Therapies

Tay-Sachs Research

GM-1 Research

Canavan Research

Sandhoff Research

Clinical Trials

Donating Tissue for Research

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Recent issues:

2016 April NTSAD Research Review

2016 March NTSAD Research Review

2016 February NTSAD Research Review


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