NTSAD Virtual Family Conference Research | Late Onset GM2 Gangliosidosis Breakout

Florian Eichler, MD
Massachusetts General Hospital
NTSAD Scientific Advisory Committee member
Addressing Clinical Trial Questions

Taylor Fields
IntraBio Clinical Trial

Dan Lewi
Apart and CATS Foundation (UK)
Report on Relevant Outcome Measures through Patient Wearable Technology

Heather Gray-Edwards, PhD
UMass Medical School
Gene Therapy Studies in Sheep