NTSAD Virtual Family Conference | 2021 Late Onset GM2 Research Breakout

Steve Walkley, PhD, Albert Einstein College of Medicine
LOTS Think Tank

Heather Gray-Edwards, PhD, UMass Medical School
Gene therapy studies in sheep

Camilo Toro, MD, NIH
Medications Do’s and Don’ts

Heather Lau, MD
Questions to ask your doctor about Clinical Trials

Taylor Fields, Senior VP
IntraBio clinical trial

Isabela A Batsu, MD, Global Project Head, Rare Disease and Rare Blood Disorder Development
Sanofi Genzyme: Late Onset GM2 Patient Journey poster