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Leading the Fight to treat and cure
Tay-Sachs, Canavan, Sandhoff, GM1 and related diseases

 
 

Donate to the Canavan Research Fund

The Canavan Research Fund of National Tay-Sachs & Allied Diseases Association, Inc. (NTSAD) is a fund created to support Canavan research. Research grants made from this fund will be directed to Canavan research specifically, and will help defray travel-related clinical trial expenses when and if needed.

You can learn more about Guangping Gao, PhD and his work on a gene therapy for Canavan Disease at the University of Massachusetts Medical Center in Worcester, Massachusetts, read this Newsweek article published in April 2016, Gene Therapy Might Be the Best, and Perhaps Only, Chance at Curing Brain Diseases. Sign up for NTSAD's Research Review e-communications to hear the latest in research news.

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What is Canavan?

Canavan is a progressive neurological genetic disorder caused by the absence of a vital enzyme known as aspartoacylase (ASPA). ASPA breaks N-acetylaspartate acid (NAA) into building blocks essential for building myelin. Myelin is a fatty membrane (also known as white matter) that forms a proactive coating around each nerve ensuring the nerve functions properly.  It is one of over 50 genetically inherited disorders known as Leukodystrophies Diseases.

What about research?

To date, there is no treatment or cure for Canavan disease but research is making exciting advances towards a treatment and a cure.  Research includes gene therapy, stem cell therapy and acetate supplement.

Read more about the Research We Fund here.

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